Afamelanotide

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Afamelanotide
DrugBank ID DB04931
Brand Names (EU) Scenesse
Evidence Level L5
Predicted Indications 50
Top Prediction Score 98.87%

Approved Indication (EMA)

Prevention of phototoxicity in adult patients with erythropoietic protoporphyria (EPP).


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 X-linked erythropoietic protoporphyria 98.87% DL
2 autosomal erythropoietic protoporphyria 98.69% DL
3 cutaneous porphyria 98.36% DL
4 erythropoietic protoporphyria 97.28% DL
5 cyclic hematopoiesis 92.87% DL
6 primary hyperoxaluria 91.33% DL
7 X-linked severe congenital neutropenia 90.67% DL
8 autosomal recessive severe congenital neutropenia due to CXCR2 deficiency 90.08% DL
9 cold agglutinin disease 90.07% DL
10 proteinuria 89.66% DL
11 autosomal recessive severe congenital neutropenia due to JAGN1 deficiency 89.13% DL
12 autosomal recessive severe congenital neutropenia due to CSF3R deficiency 89.11% DL
13 adult idiopathic neutropenia 88.72% DL
14 mixed-type autoimmune hemolytic anemia 88.70% DL
15 drug-induced autoimmune hemolytic anemia 88.64% DL
16 isolated congenital growth hormone deficiency 88.48% DL
17 primary CD59 deficiency 88.47% DL
18 progeroid syndrome, Petty type 88.40% DL
19 progeria-short stature-pigmented nevi syndrome 88.31% DL
20 neonatal autoimmune hemolytic anemia 88.17% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.