Ambrisentan

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Ambrisentan
DrugBank ID DB06403
Brand Names (EU) Volibris
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.41%

Approved Indication (EMA)

Volibris is indicated for treatment of pulmonary arterial hypertension (PAH) in adult patients of WHO Functional Class (FC) II to III, including use in combination treatment (see section 5.1).  Efficacy has been shown in idiopathic PAH (IPAH) and in PAH associated with connective tissue disease. Volibris is indicated for treatment of PAH in adolescents and children (aged 8 to less than 18 years) of WHO Functional Class (FC) II to III including use in combination treatment. Efficacy has been show


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 pulmonary arteriovenous malformation (disease) 99.41% DL
2 pulmonary arterial hypertension associated with congenital heart disease 99.37% DL
3 pulmonary arterial hypertension 99.37% DL
4 pulmonary arterial hypertension associated with schistosomiasis 99.30% DL
5 pulmonary arterial hypertension associated with HIV infection 99.30% DL
6 pulmonary arterial hypertension associated with chronic hemolytic anemia 99.30% DL
7 pulmonary arterial hypertension associated with connective tissue disease 99.30% DL
8 malformation syndrome with odontal and/or periodontal component 99.19% DL
9 hypotrichosis simplex of the scalp 99.15% DL
10 hypertrichosis (disease) 99.14% DL
11 syndrome with a Dandy-Walker malformation as major feature 99.12% DL
12 isolated genetic hair shaft abnormality 99.04% DL
13 Ambras type hypertrichosis universalis congenita 99.02% DL
14 congenital hypotrichosis milia 98.77% DL
15 diffuse alopecia areata 98.62% DL
16 alopecia 96.98% DL
17 telangiectasia, hereditary hemorrhagic, 95.48% DL
18 pulmonary hypertension, primary 92.60% DL
19 genetic alopecia 92.46% DL
20 obsolete patella aplasia, coxa vara, and tarsal synostosis 92.40% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.