Busulfan

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Busulfan
DrugBank ID DB01008
Brand Names (EU) Busulfan Fresenius Kabi
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.62%

Approved Indication (EMA)

Busulfan Fresenius Kabi followed by cyclophosphamide (BuCy2) is indicated as conditioning treatment prior to conventional haematopoietic progenitor cell transplantation (HPCT) in adult patients when the combination is considered the best available option. Busulfan Fresenius Kabi followed by cyclophosphamide (BuCy4) or melphalan (BuMel) is indicated as conditioning treatment prior to conventional haematopoietic progenitor cell transplantation in paediatric patients.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 myelodysplastic syndrome 99.62% DL
2 refractory cytopenia of childhood 99.54% DL
3 unclassified myelodysplastic syndrome 99.53% DL
4 partial deletion of the long arm of chromosome 5 99.51% DL
5 aregenerative anemia 99.49% DL
6 severe congenital hypochromic anemia with ringed sideroblasts 99.49% DL
7 HIV infectious disease 99.44% DL
8 neurodevelopmental disorder with ataxic gait, absent speech, and decreased cortical white matter 99.22% DL
9 seborrheic keratosis 99.16% DL
10 feline acquired immunodeficiency syndrome 99.06% DL
11 simian immunodeficiency virus infection 99.06% DL
12 rheumatoid arthritis 99.04% DL
13 obsolete familial combined hyperlipidemia 99.02% DL
14 female breast carcinoma 98.86% DL
15 primary cutaneous T-cell lymphoma 98.84% DL
16 vulvar inverted follicular keratosis 98.75% DL
17 multiple sclerosis 98.67% DL
18 granulomatous slack skin disease 98.58% DL
19 seborrheic dermatitis 98.52% DL
20 Crohn’s colitis 98.44% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.