Cannabidiol

Evidence Level: L5 Predicted Indications: 53

Quick Overview

Item Value
Drug Name Cannabidiol
DrugBank ID DB09061
Brand Names (EU) Epidyolex
Evidence Level L5
Predicted Indications 53
Top Prediction Score 96.17%

Approved Indication (EMA)

Epidyolex is indicated for use as adjunctive therapy of seizures associated with Lennox Gastaut syndrome (LGS) or Dravet syndrome (DS), in conjunction with clobazam, for patients 2 years of age and older.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 restless legs syndrome 96.17% DL
2 bilateral parasagittal parieto-occipital polymicrogyria 95.99% DL
3 axial spondylometaphyseal dysplasia 94.22% DL
4 amyotrophic lateral sclerosis 94.15% DL
5 trichomegaly-retina pigmentary degeneration-dwarfism syndrome 93.83% DL
6 episodic kinesigenic dyskinesia 93.73% DL
7 Mills syndrome 93.41% DL
8 amyotrophic lateral sclerosis, susceptibility to 93.40% DL
9 lower motor neuron syndrome with late-adult onset 93.21% DL
10 lethal arthrogryposis-anterior horn cell disease syndrome 93.18% DL
11 monomelic amyotrophy 93.07% DL
12 amyotrohpic lateral sclerosis type 22 92.89% DL
13 PURA-related severe neonatal hypotonia-seizures-encephalopathy syndrome due to a point mutation 92.39% DL
14 neonatal period electroclinical syndrome 92.30% DL
15 1q44 microdeletion syndrome 92.22% DL
16 myoclonic epilepsy, Hartung type 92.01% DL
17 developmental and epileptic encephalopathy 91.99% DL
18 genetic lethal multiple congenital anomalies/dysmorphic syndrome 91.92% DL
19 autosomal dominant mitochondrial myopathy with exercise intolerance 91.88% DL
20 infancy electroclinical syndrome 91.85% DL

Showing top 20 of 53 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.