Deferiprone

Evidence Level: L5 Predicted Indications: 56

Quick Overview

Item Value
Drug Name Deferiprone
DrugBank ID DB08826
Brand Names (EU) Deferiprone Lipomed, Ferriprox
Evidence Level L5
Predicted Indications 56
Top Prediction Score 99.20%

Approved Indication (EMA)

Deferiprone Lipomed monotherapy is indicated for the treatment of iron overload in patients with thalassaemia major when current chelation therapy is contraindicated or inadequate. Deferiprone Lipomed in combination with another chelator is indicated in patients with thalassaemia major when monotherapy with any iron chelator is ineffective, or when prevention or treatment of life-threatening consequences of iron overload justifies rapid or intensive correction.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 hepatic porphyria 99.20% DL
2 hepatopulmonary syndrome 99.20% DL
3 primitive portal vein thrombosis 99.20% DL
4 early-onset familial noncirrhotic portal hypertension 99.20% DL
5 hepatoportal sclerosis 99.20% DL
6 idiopathic copper-associated cirrhosis 99.20% DL
7 hemoglobinopathy 99.16% DL
8 pyruvate kinase deficiency of red cells 99.15% DL
9 beta-thalassemia with other manifestations 99.03% DL
10 pyropoikilocytosis, hereditary 99.02% DL
11 partial deletion of the short arm of chromosome 16 98.92% DL
12 hemolytic anemia due to glucophosphate isomerase deficiency 98.79% DL
13 chronic hepatitis C virus infection 98.44% DL
14 obsolete familial combined hyperlipidemia 97.16% DL
15 HIV infectious disease 96.66% DL
16 familial hyperlipidemia 96.50% DL
17 homozygous familial hypercholesterolemia 96.42% DL
18 neurodevelopmental disorder with ataxic gait, absent speech, and decreased cortical white matter 96.20% DL
19 paratenonitis 96.03% DL
20 calcific tendinitis 95.95% DL

Showing top 20 of 56 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.