Evolocumab

Evidence Level: L5 Predicted Indications: 51

Quick Overview

Item Value
Drug Name Evolocumab
DrugBank ID DB09303
Brand Names (EU) Repatha
Evidence Level L5
Predicted Indications 51
Top Prediction Score 99.82%

Approved Indication (EMA)

Hypercholesterolaemia and mixed dyslipidaemia Repatha is indicated in adults with primary hypercholesterolaemia (heterozygous familial and non-familial) or mixed dyslipidaemia, as an adjunct to diet: in combination with a statin or statin with other lipid lowering therapies in patients unable to reach LDL-C goals with the maximum tolerated dose of a statin or, alone or in combination with other lipid-lowering therapies in patients who are statin-intolerant, or for whom a statin is contraindicat


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 symptomatic form of hemophilia in female carriers 99.82% DL
2 familial apolipoprotein C-II deficiency 99.50% DL
3 thrombocytopenic purpura 99.42% DL
4 factor XI deficiency 99.29% DL
5 hemophilia A with vascular abnormality 99.22% DL
6 disease of catalytic activity 99.08% DL
7 hemorrhagic disease of newborn 98.89% DL
8 ichthyosis, X-linked, without steroid sulfatase deficiency 98.84% DL
9 inherited thrombophilia 98.82% DL
10 disorder of other vitamins and cofactors metabolism and transport 98.80% DL
11 adenosine deaminase deficiency 98.80% DL
12 xanthomatosis (disease) 98.78% DL
13 esophageal varices without bleeding 98.75% DL
14 esophageal varices with bleeding 98.75% DL
15 46,XY disorder of sexual development due to dihydrotestosterone backdoor pathway biosynthesis defect 98.73% DL
16 3-hydroxyacyl-CoA dehydrogenase deficiency 98.70% DL
17 cholesterol catabolic process disease 98.66% DL
18 coagulation protein disease 98.66% DL
19 46,XY disorder of sex development due to a cholesterol synthesis defect 98.64% DL
20 neutral lipid storage disease 98.56% DL

Showing top 20 of 51 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.