Fenfluramine Hydrochloride

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Fenfluramine Hydrochloride
DrugBank ID DB00574
Brand Names (EU) Fintepla
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.96%

Approved Indication (EMA)

Treatment of seizures associated with Dravet syndrome as an add-on therapy to other antiepileptic medicines for patients 2 years of age and older. Fintepla is indicated for the treatment of seizures associated with Dravet syndrome and Lennox-Gastaut syndrome as an add-on therapy to other anti-epileptic medicines for patients 2 years of age and older.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 obesity disorder 99.96% DL
2 proximal 16p11.2 microdeletion syndrome 99.93% DL
3 hypervitaminosis 99.92% DL
4 obsolete hypertelorism (disease) 99.86% DL
5 frontorhiny 99.78% DL
6 monogenic obesity 99.67% DL
7 pentosuria 88.16% DL
8 lethal polymalformative syndrome, Boissel type 82.78% DL
9 myopia X-linked 81.42% DL
10 retinal dystrophy with or without extraocular anomalies 79.85% DL
11 fatty liver disease 78.26% DL
12 polymicrogyria, perisylvian, with cerebellar hypoplasia and arthrogryposis 77.72% DL
13 major affective disorder 76.94% DL
14 myopia 26, X-linked, female-limited 75.30% DL
15 schizophrenia 74.62% DL
16 Charcot-Marie-Tooth disease, demyelinating, type 1G 72.87% DL
17 mitral valve prolapse, myxomatous 70.49% DL
18 hypercarotenemia and vitamin A deficiency, autosomal recessive 68.91% DL
19 hydranencephaly (disease) 68.86% DL
20 syndromic myopia 68.55% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.