Ganaxolone

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Ganaxolone
DrugBank ID DB05087
Brand Names (EU) Ztalmy
Evidence Level L5
Predicted Indications 50
Top Prediction Score 94.85%

Approved Indication (EMA)

Ztalmy is indicated for the adjunctive treatment of epileptic seizures associated with cyclin-dependent kinase-like 5 (CDKL5) deficiency disorder (CDD) in patients 2 to 17 years of age. Ztalmy may be continued in patients 18 years of age and older.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 alcohol withdrawal delirium 94.85% DL
2 hallucinogen abuse 93.07% DL
3 barbiturate abuse 93.07% DL
4 antidepressant type abuse 93.07% DL
5 phencyclidine abuse 82.76% DL
6 alcohol withdrawal 81.80% DL
7 autism spectrum disorder 79.30% DL
8 gaze palsy, familial horizontal, with progressive scoliosis 77.04% DL
9 asperger syndrome, susceptibility to 76.13% DL
10 autism susceptibility 1 75.45% DL
11 drug dependence 74.69% DL
12 alcohol-related disorders 73.30% DL
13 amelocerebrohypohidrotic syndrome 73.06% DL
14 Wernicke-Korsakoff syndrome 72.65% DL
15 autism, susceptibility to 72.05% DL
16 intellectual disability 70.95% DL
17 adenosarcoma 70.71% DL
18 uterine ligament adenosarcoma 70.67% DL
19 16q24.3 microdeletion syndrome 70.06% DL
20 chromosome 15q11.2 deletion syndrome 69.93% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.