Ivosidenib

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Ivosidenib
DrugBank ID DB14568
Brand Names (EU) Tibsovo
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.54%

Approved Indication (EMA)

Tibsovo in combination with azacitidine is indicated for the treatment of adult patients with newly diagnosed acute myeloid leukaemia (AML) with an isocitrate dehydrogenase-1 (IDH1) R132 mutation who are not eligible to receive standard induction chemotherapy (see section 5.1). Tibsovo monotherapy is indicated for the treatment of adult patients with locally advanced or metastatic cholangiocarcinoma with an IDH1 R132 mutation who were previously treated by at least one prior line of systemic the


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 acute myeloid leukemia with t(8;21)(q22;q22) translocation 99.54% DL
2 acute myeloid leukemia with CEBPA somatic mutations 99.53% DL
3 acute myeloid leukemia and myelodysplastic syndromes related to topoisomerase type 2 inhibitor 99.52% DL
4 acute myeloid leukemia with inv3(p21;q26.2) or t(3;3)(p21;q26.2) 99.51% DL
5 therapy related acute myeloid leukemia and myelodysplastic syndrome 99.36% DL
6 bulbar polio 99.31% DL
7 acute myeloid leukemia with t(8;16)(p11;p13) translocation 99.26% DL
8 acute myeloid leukemia and myelodysplastic syndromes related to radiation 99.26% DL
9 acute myeloid leukemia and myelodysplastic syndromes related to alkylating agent 99.26% DL
10 acute myeloid leukemia with t(9;11)(p22;q23) 99.16% DL
11 inherited acute myeloid leukemia 99.13% DL
12 unclassified acute myeloid leukemia 99.11% DL
13 acute myeloid leukemia with t(6;9)(p23;q34) 99.08% DL
14 acute myeloblastic leukemia with maturation 99.04% DL
15 acute myeloblastic leukemia without maturation 98.99% DL
16 5q35 microduplication syndrome 98.97% DL
17 acute myeloid leukemia with minimal differentiation 98.86% DL
18 neuralgic amyotrophy 98.80% DL
19 acute myeloid leukemia with NPM1 somatic mutations 98.76% DL
20 amyotrophic neuralgia 98.73% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.