Leflunomide

Evidence Level: L5 Predicted Indications: 51

Quick Overview

Item Value
Drug Name Leflunomide
DrugBank ID DB01097
Brand Names (EU) Arava, Leflunomide medac
Evidence Level L5
Predicted Indications 51
Top Prediction Score 99.97%

Approved Indication (EMA)

Leflunomide is indicated for the treatment of adult patients with: active rheumatoid arthritis as a ‘disease-modifying antirheumatic drug’ (DMARD); active psoriatic arthritis. Recent or concurrent treatment with hepatotoxic or haematotoxic DMARDs (e.g. methotrexate) may result in an increased risk of serious adverse reactions; therefore, the initiation of leflunomide treatment has to be carefully considered regarding these benefit / risk aspects. Moreover, switching from leflunomide to another


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 rheumatoid arthritis 99.97% DL
2 brachydactyly-syndactyly syndrome 99.93% DL
3 colobomatous microphthalmia-rhizomelic dysplasia syndrome 99.93% DL
4 indolent plasma cell myeloma 95.47% DL
5 plasma cell myeloma 95.16% DL
6 myeloid leukemia 92.99% DL
7 Meester-Loeys syndrome 86.55% DL
8 ganglioneuroblastoma (disease) 76.30% DL
9 WHIM syndrome 75.88% DL
10 scalp dermatosis 73.87% DL
11 vertebral anomalies and variable endocrine and T-cell dysfunction 72.25% DL
12 retroperitoneal neoplasm 71.43% DL
13 obsolete susceptibility to ischemic stroke 70.51% DL
14 neuroblastoma 64.84% DL
15 gout 63.94% DL
16 polydipsia 62.14% DL
17 congenital temporomandibular joint ankylosis 61.70% DL
18 cholangiocarcinoma, susceptibility to 60.31% DL
19 anuria 59.24% DL
20 osteoarthritis susceptibility 57.89% DL

Showing top 20 of 51 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.