Luspatercept

Evidence Level: L5 Predicted Indications: 52

Quick Overview

Item Value
Drug Name Luspatercept
DrugBank ID DB12281
Brand Names (EU) Reblozyl
Evidence Level L5
Predicted Indications 52
Top Prediction Score 96.32%

Approved Indication (EMA)

Reblozyl is indicated in adults for the treatment of transfusion-dependent anaemia due to very low, low and intermediate-risk myelodysplastic syndromes (MDS).Reblozyl is indicated in adults for the treatment of anaemia associated with transfusion dependent and non transfusion dependent beta thalassaemia.  Reblozyl is indicated in adults for the treatment of transfusion-dependent anaemia due to very low, low and intermediate-risk myelodysplastic syndromes (MDS).Reblozyl is indicated in adult


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 dominant beta-thalassemia 96.32% DL
2 monosomy X 96.00% DL
3 hepatic infarction 95.70% DL
4 hepatic veno-occlusive disease 94.91% DL
5 peliosis hepatis 94.75% DL
6 syndrome with combined immunodeficiency 94.28% DL
7 pyruvate kinase deficiency of red cells 93.84% DL
8 thalassemia, beta+, silent allele 93.32% DL
9 familial apolipoprotein C-II deficiency 93.05% DL
10 adenosine deaminase deficiency 92.86% DL
11 Hb Bart’s hydrops fetalis 92.75% DL
12 beta-thalassemia with other manifestations 92.61% DL
13 mitochondrial oxidative phosphorylation disorder due to nuclear DNA anomalies 92.34% DL
14 partial deletion of the short arm of chromosome 16 92.14% DL
15 hemolytic anemia due to glucophosphate isomerase deficiency 91.92% DL
16 liver angiosarcoma 91.84% DL
17 pyropoikilocytosis, hereditary 91.80% DL
18 reticular dysgenesis 91.66% DL
19 beta thalassemia 91.57% DL
20 severe combined immunodeficiency due to LCK deficiency 91.50% DL

Showing top 20 of 52 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.