Midostaurin

Evidence Level: L5 Predicted Indications: 56

Quick Overview

Item Value
Drug Name Midostaurin
DrugBank ID DB06595
Brand Names (EU) Rydapt
Evidence Level L5
Predicted Indications 56
Top Prediction Score 98.92%

Approved Indication (EMA)

Rydapt is indicated: in combination with standard daunorubicin and cytarabine induction and high dose cytarabine consolidation chemotherapy, and for patients in complete response followed by Rydapt single agent maintenance therapy, for adult patients with newly diagnosed acute myeloid leukaemia (AML) who are FLT3 mutation positive (see section 4.2); as monotherapy for the treatment of adult patients with aggressive systemic mastocytosis (ASM), systemic mastocytosis with associated haematologica


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 familial thrombocytosis 98.92% DL
2 reactive thrombocytosis 98.76% DL
3 metastatic melanoma 97.64% DL
4 inverse Klippel-Trenaunay syndrome 97.62% DL
5 thrombocythemia 97.48% DL
6 non-cutaneous melanoma 97.13% DL
7 epithelioid cell melanoma 96.95% DL
8 eyelid melanoma 96.94% DL
9 scrotum melanoma 96.73% DL
10 acute myeloid leukemia with t(8;21)(q22;q22) translocation 96.39% DL
11 superficial spreading melanoma 96.39% DL
12 lentigo maligna melanoma 96.39% DL
13 CDK4 linked melanoma 96.39% DL
14 acral lentiginous melanoma (disease) 96.39% DL
15 balloon cell malignant melanoma 96.39% DL
16 amelanotic skin melanoma 96.39% DL
17 nodular malignant melanoma 96.39% DL
18 malignant melanoma of the mucosa 96.39% DL
19 choroideremia 96.38% DL
20 acute myeloid leukemia with inv3(p21;q26.2) or t(3;3)(p21;q26.2) 96.37% DL

Showing top 20 of 56 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.