Pemigatinib

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Pemigatinib
DrugBank ID DB15102
Brand Names (EU) Pemazyre
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.71%

Approved Indication (EMA)

Pemazyre monotherapy is indicated for the treatment of adults with locally advanced or metastatic cholangiocarcinoma with a fibroblast growth factor receptor 2 (FGFR2) fusion or rearrangement that have progressed  after at least one prior line of systemic therapy.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 multiple endocrine neoplasia 99.71% DL
2 amenorrhea (disease) 99.54% DL
3 HER2 positive breast carcinoma 99.49% DL
4 cytomegalovirus infection 99.46% DL
5 malignant catarrh 99.43% DL
6 infectious bovine rhinotracheitis 99.43% DL
7 amyotrophic lateral sclerosis 99.41% DL
8 amyotrohpic lateral sclerosis type 22 99.27% DL
9 amyotrophic lateral sclerosis, susceptibility to 99.25% DL
10 axial spondylometaphyseal dysplasia 99.25% DL
11 Mills syndrome 99.22% DL
12 progesterone-receptor negative breast cancer 99.18% DL
13 progesterone-receptor positive breast cancer 99.17% DL
14 normal breast-like subtype of breast carcinoma 99.17% DL
15 trichomegaly-retina pigmentary degeneration-dwarfism syndrome 99.17% DL
16 breast tumor luminal A or B 99.15% DL
17 lethal arthrogryposis-anterior horn cell disease syndrome 99.12% DL
18 bilateral parasagittal parieto-occipital polymicrogyria 99.09% DL
19 lower motor neuron syndrome with late-adult onset 99.08% DL
20 monomelic amyotrophy 99.03% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.