Pitolisant

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Pitolisant
DrugBank ID DB11642
Brand Names (EU) Wakix
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.71%

Approved Indication (EMA)

Wakix is indicated in adults, adolescents and children from the age of 6 years for the treatment of narcolepsy with or without cataplexy (see also section 5.1).


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 insomnia (disease) 99.71% DL
2 attention deficit-hyperactivity disorder 99.36% DL
3 faciodigitogenital syndrome 99.29% DL
4 X-linked adrenoleukodystrophy 99.03% DL
5 disorder of peroxisomal alpha-, beta- and omega-oxidation 98.87% DL
6 ACBD5 deficiency 98.65% DL
7 Creutzfeldt-Jakob disease 98.55% DL
8 narcolepsy-cataplexy syndrome 98.49% DL
9 narcolepsy 98.42% DL
10 narcolepsy, susceptibility to 98.21% DL
11 megaconial type congenital muscular dystrophy 97.64% DL
12 hypersomnia (disease) 96.98% DL
13 Balo concentric sclerosis 96.90% DL
14 circadian rhythm sleep disorder 96.73% DL
15 chondromyxoid fibroma 96.61% DL
16 narcolepsy without cataplexy 94.96% DL
17 variably protease-sensitive prionopathy 94.78% DL
18 central nervous system disease 94.77% DL
19 attention deficit hyperactivity disorder, inattentive type 94.48% DL
20 Wernicke-Korsakoff syndrome 93.65% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.