Rasburicase

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Rasburicase
DrugBank ID DB00049
Brand Names (EU) Fasturtec
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.99%

Approved Indication (EMA)

Treatment and prophylaxis of acute hyperuricaemia, in order to prevent acute renal failure, in adults, children and adolescents (aged 0 to 17 years) with haematological malignancy with a high tumour burden and at risk of a rapid tumour lysis or shrinkage at initiation of chemotherapy.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 obsolete hyperuricemia (disease) 99.99% DL
2 hypouricemia, renal 99.99% DL
3 hypoxanthine guanine phosphoribosyltransferase partial deficiency 99.97% DL
4 hepatic porphyria 99.97% DL
5 primitive portal vein thrombosis 99.97% DL
6 hepatoportal sclerosis 99.97% DL
7 hepatopulmonary syndrome 99.97% DL
8 early-onset familial noncirrhotic portal hypertension 99.97% DL
9 idiopathic copper-associated cirrhosis 99.97% DL
10 renal tubular acidosis 99.85% DL
11 disorder of phenylalanine metabolism 99.83% DL
12 disorder of tyrosine metabolism 99.69% DL
13 teratogenic Pierre Robin syndrome 99.68% DL
14 glycogen storage disease due to hepatic glycogen synthase deficiency 99.58% DL
15 Lesch-Nyhan syndrome 99.58% DL
16 tetrahydrobiopterin-responsive hyperphenylalaninemia/phenylketonuria 99.47% DL
17 G6PD deficiency 99.00% DL
18 inborn disorder of gamma-aminobutyric acid metabolism 97.73% DL
19 inborn disorder of ornithine metabolism 97.68% DL
20 inborn disorder of amino acid and other organic acid metabolism 97.66% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.