Riluzole

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Riluzole
DrugBank ID DB00740
Brand Names (EU) Rilutek
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.99%

Approved Indication (EMA)

Rilutek is indicated to extend life or the time to mechanical ventilation for patients with amyotrophic lateral sclerosis (ALS). Clinical trials have demonstrated that Rilutek extends survival for patients with ALS. Survival was defined as patients who were alive, not intubated for mechanical ventilation and tracheotomy-free. There is no evidence that Rilutek exerts a therapeutic effect on motor function, lung function, fasciculations, muscle strength and motor symptoms. Rilutek has not been sho


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 bilateral parasagittal parieto-occipital polymicrogyria 99.99% DL
2 amyotrophic lateral sclerosis 99.99% DL
3 axial spondylometaphyseal dysplasia 99.99% DL
4 lower motor neuron syndrome with late-adult onset 99.99% DL
5 trichomegaly-retina pigmentary degeneration-dwarfism syndrome 99.99% DL
6 lethal arthrogryposis-anterior horn cell disease syndrome 99.99% DL
7 monomelic amyotrophy 99.99% DL
8 Mills syndrome 99.98% DL
9 amyotrophic lateral sclerosis, susceptibility to 99.98% DL
10 autosomal dominant mitochondrial myopathy with exercise intolerance 99.98% DL
11 amyotrohpic lateral sclerosis type 22 99.98% DL
12 polymicrogyria, perisylvian, with cerebellar hypoplasia and arthrogryposis 99.70% DL
13 hydranencephaly (disease) 99.67% DL
14 congenital disorder of glycosylation with defective fucosylation 99.67% DL
15 schizophrenia 99.66% DL
16 retinal dystrophy with or without extraocular anomalies 99.64% DL
17 atypical glycine encephalopathy 99.62% DL
18 Charcot-Marie-Tooth disease, demyelinating, type 1G 99.59% DL
19 myopia 26, X-linked, female-limited 99.55% DL
20 syndromic myopia 99.54% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.