Romiplostim

Evidence Level: L5 Predicted Indications: 51

Quick Overview

Item Value
Drug Name Romiplostim
DrugBank ID DB05332
Brand Names (EU) Nplate
Evidence Level L5
Predicted Indications 51
Top Prediction Score 100.00%

Approved Indication (EMA)

Adults: Nplate is indicated for the treatment of primary immune thrombocytopenia  (ITP) in adult patients who are refractory to other treatments (e.g. corticosteroids, immunoglobulins). Paediatrics: Nplate is indicated for the treatment of chronic primary immune thrombocytopenia (ITP) in paediatric patients one year of age and older who are refractory to other treatments (e.g. corticosteroids, immunoglobulins).


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 primary release disorder of platelets 100.00% DL
2 pseudo-von Willebrand disease 100.00% DL
3 Glanzmann thrombasthenia 100.00% DL
4 fetal and neonatal alloimmune thrombocytopenia 99.99% DL
5 Scott syndrome 99.97% DL
6 hemorrhagic disorder due to a constitutional thrombocytopenia 99.95% DL
7 bleeding diathesis due to a collagen receptor defect 99.95% DL
8 platelet-type bleeding disorder 99.93% DL
9 autosomal dominant macrothrombocytopenia 99.88% DL
10 Ehlers-Danlos syndrome, fibronectinemic type 99.85% DL
11 paroxysmal nocturnal hemoglobinuria 99.64% DL
12 proteinuria 99.58% DL
13 neurolymphomatosis 99.57% DL
14 mixed-type autoimmune hemolytic anemia 99.56% DL
15 drug-induced autoimmune hemolytic anemia 99.53% DL
16 neonatal autoimmune hemolytic anemia 99.49% DL
17 plasmacytoma 99.49% DL
18 primary CD59 deficiency 99.44% DL
19 Peyronie disease 99.34% DL
20 cold agglutinin disease 99.26% DL

Showing top 20 of 51 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.