Setmelanotide

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Setmelanotide
DrugBank ID DB11700
Brand Names (EU) Imcivree
Evidence Level L5
Predicted Indications 50
Top Prediction Score 92.25%

Approved Indication (EMA)

IMCIVREE is indicated for the treatment of obesity and the control of hunger associated with genetically confirmed Bardet Biedl syndrome (BBS), loss-of-function biallelic pro-opiomelanocortin (POMC), including PCSK1, deficiency or biallelic leptin receptor (LEPR) deficiency in adults and children 2 years of age and above.


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 migraine disorder 92.25% DL
2 migraine with brainstem aura 91.68% DL
3 non-syndromic esophageal malformation 89.60% DL
4 esophageal disease 88.38% DL
5 amenorrhea (disease) 86.01% DL
6 cauda equina syndrome 83.00% DL
7 obsolete neurogenic bladder (disease) 82.21% DL
8 esophageal ulcer 81.44% DL
9 Ambras type hypertrichosis universalis congenita 81.23% DL
10 pituitary dwarfism 81.07% DL
11 migraine with or without aura, susceptibility to 80.37% DL
12 atrophoderma vermiculata 79.98% DL
13 malformation syndrome with odontal and/or periodontal component 78.91% DL
14 syndrome with a Dandy-Walker malformation as major feature 78.38% DL
15 isolated genetic hair shaft abnormality 78.00% DL
16 erectile dysfunction (disease) 77.93% DL
17 hypertrichosis (disease) 77.89% DL
18 ulerythema ophryogenesis 76.67% DL
19 acne (disease) 74.14% DL
20 adrenal gland hyperfunction 72.82% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.