Thalidomide

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Thalidomide
DrugBank ID DB01041
Brand Names (EU) Thalidomide BMS (previously Thalidomide Celgene)
Evidence Level L5
Predicted Indications 50
Top Prediction Score 98.96%

Approved Indication (EMA)

Thalidomide BMS in combination with melphalan and prednisone as first line treatment of patients with untreated multiple myeloma, aged >/= 65 years or ineligible for high dose chemotherapy. Thalidomide BMS is prescribed and dispensed according to the Thalidomide Celgene Pregnancy Prevention Programme (see section 4.4).


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 ganglioneuroblastoma (disease) 98.96% DL
2 vertebral anomalies and variable endocrine and T-cell dysfunction 98.95% DL
3 retroperitoneal neoplasm 98.68% DL
4 neuroblastoma 98.66% DL
5 brachydactyly-syndactyly syndrome 94.22% DL
6 colobomatous microphthalmia-rhizomelic dysplasia syndrome 93.20% DL
7 rheumatoid arthritis 92.40% DL
8 myeloid leukemia 90.54% DL
9 indolent plasma cell myeloma 88.46% DL
10 plasma cell myeloma 85.34% DL
11 acute lymphoblastic leukemia (disease) 74.75% DL
12 cholangiocarcinoma, susceptibility to 64.32% DL
13 GCGR-related hyperglucagonemia 60.49% DL
14 scalp dermatosis 59.90% DL
15 congenital temporomandibular joint ankylosis 59.59% DL
16 polydipsia 59.20% DL
17 mitral valve prolapse, myxomatous 58.87% DL
18 epidural abscess 57.97% DL
19 giant cell reparative granuloma 57.02% DL
20 pancreas, dorsal, agenesis of 56.94% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.