Tofacitinib

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Tofacitinib
DrugBank ID DB08895
Brand Names (EU) Xeljanz
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.27%

Approved Indication (EMA)

Rheumatoid arthritisTofacitinib in combination with methotrexate (MTX) is indicated for the treatment of moderate to severe active rheumatoid arthritis (RA) in adult patients who have responded inadequately to, or who are intolerant to one or more disease-modifying antirheumatic drugs (DMARDs) (see section 5.1). Tofacitinib can be given as monotherapy in case of intolerance to MTX or when treatment with MTX is inappropriate (see sections 4.4 and 4.5). Psoriatic arthritisTofacitinib in combinatio


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 rheumatoid arthritis 99.27% DL
2 colobomatous microphthalmia-rhizomelic dysplasia syndrome 98.96% DL
3 brachydactyly-syndactyly syndrome 98.88% DL
4 indolent plasma cell myeloma 96.66% DL
5 plasma cell myeloma 96.09% DL
6 myeloid leukemia 95.43% DL
7 ganglioneuroblastoma (disease) 79.55% DL
8 marcothrombocytopenia with mitral valve insufficiency 76.17% DL
9 hereditary thrombocytopenia with normal platelets 75.76% DL
10 vertebral anomalies and variable endocrine and T-cell dysfunction 75.34% DL
11 retroperitoneal neoplasm 75.26% DL
12 transient neonatal thrombocytopenia 73.38% DL
13 dense granule disease 70.66% DL
14 Meester-Loeys syndrome 65.68% DL
15 neuroblastoma 65.05% DL
16 stroke disorder 62.11% DL
17 thrombocytopenia 61.29% DL
18 atrial flutter (disease) 60.31% DL
19 cholangiocarcinoma, susceptibility to 59.92% DL
20 platelet storage pool deficiency 59.84% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.