Trametinib

Evidence Level: L5 Predicted Indications: 50

Quick Overview

Item Value
Drug Name Trametinib
DrugBank ID DB08911
Brand Names (EU) Mekinist
Evidence Level L5
Predicted Indications 50
Top Prediction Score 99.54%

Approved Indication (EMA)

Melanoma Trametinib as monotherapy or in combination with dabrafenib is indicated for the treatment of adult patients with unresectable or metastatic melanoma with a BRAF V600 mutation (see sections 4.4 and 5.1). Trametinib monotherapy has not demonstrated clinical activity in patients who have progressed on a prior BRAF inhibitor therapy (see section 5.1). Adjuvant treatment of melanoma Trametinib in combination with dabrafenib is indicated for the adjuvant treatment of adult patients with Stag


Predicted New Indications

TxGNN model predictions for potential drug repurposing:

Rank Indication Score Source
1 metastatic melanoma 99.54% DL
2 choroideremia 99.31% DL
3 non-cutaneous melanoma 99.30% DL
4 epithelioid cell melanoma 99.28% DL
5 eyelid melanoma 99.26% DL
6 scrotum melanoma 99.21% DL
7 CDK4 linked melanoma 99.14% DL
8 acral lentiginous melanoma (disease) 99.14% DL
9 amelanotic skin melanoma 99.14% DL
10 balloon cell malignant melanoma 99.14% DL
11 nodular malignant melanoma 99.14% DL
12 lentigo maligna melanoma 99.14% DL
13 superficial spreading melanoma 99.14% DL
14 malignant melanoma of the mucosa 99.14% DL
15 choroidal dystrophy, central areolar 98.97% DL
16 intestinal obstruction in the newborn due to guanylate cyclase 2C deficiency 98.74% DL
17 bilateral parasagittal parieto-occipital polymicrogyria 92.41% DL
18 amyotrophic lateral sclerosis 92.28% DL
19 anus leiomyosarcoma 91.47% DL
20 uterine corpus epithelioid leiomyosarcoma 91.31% DL

Showing top 20 of 50 predictions.


About TxGNN Predictions

Prediction Sources

Source Description
KG Knowledge Graph - Network topology-based associations
DL Deep Learning - Neural network score prediction

Evidence Levels

Level Definition
L1 Multiple Phase 3 RCTs / Systematic Reviews
L2 Single RCT or multiple Phase 2 trials
L3 Observational studies / Large case series
L4 Preclinical / Mechanistic / Case reports
L5 AI prediction only (current)

Clinical Validation Needed

Research Use Only: These predictions are computational hypotheses that require clinical validation. They should NOT be used for clinical decision-making.

Next Steps for Validation

  1. Literature Review: Search PubMed for existing evidence
  2. Clinical Trial Search: Check ClinicalTrials.gov for ongoing studies
  3. Mechanistic Analysis: Evaluate biological plausibility
  4. Preclinical Studies: Conduct in vitro/in vivo validation
  5. Clinical Trials: Design and conduct human studies

Data Access


Citation

If using this data, please cite:

@article{huang2023txgnn,
  title={A foundation model for clinician-centered drug repurposing},
  author={Huang, Kexin and others},
  journal={Nature Medicine},
  year={2023},
  doi={10.1038/s41591-023-02233-x}
}

Disclaimer: This report is for research purposes only and does not constitute medical advice. Drug repurposing predictions require rigorous clinical validation before any therapeutic application.

Copyright © 2026 EuTxGNN Project. For research purposes only. Not medical advice.